Fabry Disease

This page contains recent news articles, when available, and an overview of Fabry Disease but does not offer medical advice. You should contact your physician with regard to any health issues or concerns.

News: Fabry Disease

UPDATE 1-Genzyme says FDA declines to approve Pompe disease drug  -  ‎Nov 16, 2009‎
Reuters...area will not delay shipments of Cerezyme, though it may have a brief impact on shipments of Fabrazyme, the company's treatment for Fabry disease. ...

Vials of 5 Genzyme Drugs for Rare Diseases May Be Tainted  -  ‎Nov 21, 2009‎
Citizens ReportThe drugs affected include Cerezyme for the treatment of Gaucher disease, Fabrazyme for Fabry disease, Myozyme for Pomp disease, Aldurazyme for ...

Amicus shares fall on closed partnership, job cuts  -  ‎Oct 30, 2009‎
The Associated PressThe disorders include up to 40 rare, inherited metabolic conditions such as Fabry disease. Amicus regained exclusive worldwide rights to develop and sell ...

Reversal of First-Degree Atrioventricular Block in Fabry Disease  -  ‎Nov 9, 2009‎
Archives of Internal MedicineFabry disease is an X-linked disorder of glycosphingolipid catabolism that results from deficient activity of the lysosomal enzyme -galactosidase A in the ...

FDA warns five Genzyme drugs could be contaminated  -  ‎Nov 13, 2009‎
Bizjournals.comThe affected products include Cerezyme for Gaucher disease, Fabrazyme for Fabry disease, Myozyme for Pompe disease, Aldurazyme for Mucoploysaccharidosis ...

Shire Subpoenaed In US Drug Marketing Probe  -  ‎Oct 30, 2009‎
Wall Street JournalThe FDA is also reviewing Replagal, a Shire drug for Fabry disease, a similar genetic condition. Both Fabry and Gaucher are characterized by an inability to ...

Genzyme Stops Development Of Advanced Phosphate Binder - Update  -  ‎Nov 18, 2009‎
RTT News...manufacturing facility in Boston that resulted in restricted supplies of the company's Gaucher disease drug Cerezyme and Fabry disease drug Fabrazyme. ...

UPDATE 1-U.S. FDA: Some Genzyme drugs contaminated  -  ‎Nov 13, 2009‎
路透中国The FDA said the affected products included Cerezyme for Gaucher disease, Fabrazyme for Fabry disease, Myozyme for Pompe disease, Aldurazyme for ...

Genzyme: Focusing on Lumizyme Approval  -  ‎Oct 30, 2009‎
Seeking Alpha (blog)...the company's Allston manufacturing plant, which is where its blockbuster Gaucher disease drug Cerezyme and Fabry disease drug Fabrazyme are produced. ...

Refocusing on Therapeutic Protein Production in Plants  -  ‎Nov 20, 2009‎
Genetic Engineering News (press release)Protalix has three other plant cell-produced enzymes in its preclinical pipeline: PRX-12, a galactosidase enzyme-replacement therapy for Fabry disease; ...

Amicus Therapeutics to Present at the Lazard Capital Markets 6th Annual ...  -  ‎Nov 12, 2009‎
CNNMoney.com (press release)...diseases including lysosomal storage disorders and diseases of neurodegeneration. Amicus' lead program is in Phase 3 for the treatment of Fabry disease.

Genzyme manufacturing plant gets EU OK  -  ‎Nov 3, 2009‎
Mass High TechShortages of the two principal drugs made at the plant, Fabrazyme for Fabry disease and Cerezyme for Gaucher disease, continue following the closure of the ...

Plummeting Adderall XR sales drag on Shire's quarter  -  ‎Nov 3, 2009‎
Pharma Times...alfa for the treatment of Gaucher disease on both sides of the Atlantic as well as Replagal (agalsidase alfa) for Fabry disease in the US in 2010. ...

AMICUS THERAPEUTICS, INC. Reports Operating Results (10-Q)  -  ‎Nov 4, 2009‎
GuruFocus.comAmicus has completed Phase 2 clinical trials of Amigal(TM) for the treatment of Fabry disease and is conducting Phase 2 clinical trials of Plicera(TM) for ...

The World Biotech Market Report By Bharatbook.com  -  ‎Nov 5, 2009‎
PRMinds (press release)...market into targeting a huge range of diseases from growth deficiency to arthritis, to multiple sclerosis and orphan diseases such as Fabry's disease. ...

Amicus Therapeutics, Inc. - Pharmaceuticals & Healthcare - Deals and Alliances ...  -  ‎Nov 15, 2009‎
PR-Inside.com (Pressemitteilung)The Company's products in development are Amigal (migalastat hydrochloride) for Fabry disease, Plicera (isofagomine tartrate) for Gaucher disease and AT2220 ...

Allergan Q3 Profit Rises; Lifts FY09 Adj. EPS Outlook - Update  -  ‎Oct 29, 2009‎
Trading Markets (press release)...manufacturing facility in Boston that resulted in restricted supplies of the company's Gaucher disease drug Cerezyme and Fabry disease drug Fabrazyme. ...

La FDA informa que encuentra metal, goma y fibra en algunas partidas de ...  -  ‎Nov 17, 2009‎
Noticias Médicas (Comunicado de prensa)Jerry Walter, presidente de la National Fabry Disease Foundation, ha declarado que los pacientes afectados han visto disminuida su dosis de seis o siete a ...

Shire To Seek US Replagal Nod As Genzyme Falters  -  ‎Aug 5, 2009‎
Wall Street JournalShire's Replagal is on sale in Europe for patients with Fabry disease but not in the US There, patients are prescribed Genzyme's Fabrazyme.

Shire looking beyond attention-deficit drugs  -  ‎Aug 14, 2009‎
Philadelphia InquirerIn 2005, Shire bought Boston's Transkaryotic Therapies Inc. for $1.6 billion and now markets several of its drugs, including Replagal for Fabry disease and

Genzyme Falls After Lower Forecast Forced by Plant  -  ‎Jul 22, 2009‎
BloombergIt treats Fabry disease, an inherited illness in which lipids build up to harmful levels in the eyes, kidneys, nervous system and cardiovascular system.

FDA seeks contingency details from Genzyme  -  ‎Aug 12, 2009‎
Boston GlobeFabrazyme treats Fabry disease, in which a missing or faulty enzyme prevents the body from breaking down oils, waxes, and fatty acids that build up in the

Genzyme tosses some Allston material, sees charge  -  ‎Aug 10, 2009‎
ForbesFabrazyme treats an inherited disorder known as Fabry disease, which is caused by the buildup of a particular type of fat in the body's cells.

EMEA Issues Treatment Recommendations to Preserve Supply of ...  -  ‎Aug 14, 2009‎
Genetic Engineering News (press release)The Allston site also manufactures Genzyme's Fabry disease treatment, Fabrazyme. Shipments of Fabrazyme were not restricted following the shutdown of the

About this author:  -  ‎Aug 6, 2009‎
Seeking AlphaIn its early years, the company focused on therapies targeting the lysosomal storage disorders, including Gaucher disease, Fabry disease and Pompe disease.

Amicus Therapeutics Announces Second Quarter 2009 Financial Results  -  ‎Aug 5, 2009‎
PR Newswire (press release)As previously announced, the Phase 3 trial will evaluate the efficacy, safety, and pharmacodynamics of Amigal in males and females with Fabry disease.

Fabry trial set to answer “political problem?  -  ‎Aug 6, 2009‎
CMAJFabry disease is a rare hereditary genetic condition in which a deficiency of the enzyme alpha galactosidase A causes a buildup for a glycolipid in blood

Enzyme therapy for Fabry patients in jeopardy  -  ‎Aug 4, 2009‎
CMAJCanadians with Fabry disease face an uncertain future because an unusual government-and-industry-funded clinical trial, which provides access to a $300 000

Genetic disorder could cause strokes  -  ‎Aug 7, 2009‎
The News InternationalThe disorder known as Fabry disease is characterised by attacks of burning pain in the hands and feet, dark nodular skin lesions and progressive renal

Citi: Shire good target for Teva  -  ‎Aug 13, 2009‎
GlobesVyvance, as well as Shire's innovative TKT pipeline for treating rare diseases, including Gaucher disease, Fabry disease & Hunter disease.

FDA to Genzyme: plant not OK  -  ‎Jul 31, 2009‎
Bizjournals.comThe facility produces the drug Fabrazyme, to treat Fabry disease, and Cerezyme, to treat Gaucher's disease. Genzyme officials say they will work with the

Shire 2Q Op Income -53% On Generics; Reaffirms 09 Guidance  -  ‎Aug 5, 2009‎
Wall Street JournalFabrazyme, a Genzyme treatment for Fabry disease, was also affected. At 1128 GMT, Shire shares were down 0.3%, or 3 pence at 879p in a broadly higher London

Genzyme cuts forecasts on production problems  -  ‎Jul 28, 2009‎
PharmafocusWhen it reopens the plant will resume production of Cerezyme and Fabrazyme (agalsidase beta) for Fabry disease, but Genzyme will no longer make the third

Where Drugs Come From, and How. Once More, With A Roll of the Eyes  -  ‎Jul 31, 2009‎
CoranteOr Fabry disease? Mucopolysaccharidosis I? People who actually know something about the drug industry will be nodding their heads, though, because they'll

Genzyme Corporation hit by Shareholder Lawsuit  -  ‎Aug 3, 2009‎
PR-Inside.com (Pressemitteilung)...update its computerized manufacturing system for Fabrazyme, a treatment for Fabry disease, and ran an aseptic filling line at an unvalidated line speed.

Companies Step In to Fill Gap in Enzyme Replacement Therapy for ...  -  ‎Jul 23, 2009‎
Genetic Engineering News (press release)...the company said that it anticipate the period of constraint for two recombinant proteins (Fabrazyme for the treatment of Fabry disease and Cerezyme) to

BUYINS.NET: FCH, ARGN, MGAM, NHWK, INAP, FOLD Expected To Be Lower ...  -  ‎Jul 30, 2009‎
Trading Markets (press release)The companyas products include Amigal, which has completed Phase II clinical trial for the treatment of Fabry disease; Plicera, a Phase II clinical trial

BUYINS.NET: PEP, MO, GENZ, ISRG, STLD, OSIP Expected To Be Higher ...  -  ‎Jul 20, 2009‎
Trading Markets (press release)Fabrazyme, a recombinant form of the human enzyme alpha- galactosidase for the treatment of Fabry disease; Myozyme as a therapy for Pompe disease;

Adderall XR sales sink as Shire enthuses over new products  -  ‎Aug 6, 2009‎
Pharma TimesReplagal (agalsidase alfa), for the treatment of Fabry disease, contributed $44.4 million to the coffers, down 1%, while the ulcerative colitis therapy

Genzyme第二季盈利增长逾一?  -  ‎Jul 22, 2009‎
新浪网...肾病治疗?Renagel与Renvela的销售?增长4%,至1.75亿美元;法布里病(Fabry disease)治疗?物Fabrazyme销售?增长6%,至1.34亿美元。 ???本与开支下?了10%,至9.80

Amicus Therapeutics Announces Fourth Quarter and Full Year 2008 ...  -  06 Feb 2009
PR Newswire (press release),As previously announced, the Company plans to initiate Phase 3 development of Amigal for the treatment of Fabry disease in the second quarter of 2009.

Rindge teen receives horse thanks to gift from Make-A-Wish Foundation  -  Jan 29, 2009
The Keene Sentinel,Ten years ago Hill was diagnosed with Fabry disease, a rare genetic disorder that causes fat to build up around vital organs including the eyes, brain,

Amicus Therapeutics Announces Positive Progress of Three Lead ...  -  Jan 12, 2009
PR Newswire (press release),Amicus has completed Phase 2 clinical trials of Amigal for the treatment of Fabry disease and is conducting Phase 2 clinical trials of Plicera for the

Business briefs  -  Feb 5, 2009
Worcester Telegram,CAMBRIDGE — Genzyme Corp. recalled four batches of Fabrazyme, an enzyme replacement treatment for Fabry disease, in Europe because vials were incompletely

Genzyme Reports Strong Fourth-Quarter and 2008 Revenue Growth  -  Jan 13, 2009
WELT ONLINE,...in the post-marketing FIELD study of Fabrazyme, which is exploring additional dosing options that may facilitate earlier treatment of Fabry disease.

Genzyme shares rise on FDA panel recommendation  -  Dec 10, 2008
Forbes,Those drugs include kidney-disease treatments Renagel and Renvela, and the Fabry disease treatment Fabrazyme. Fabry disease is an inherited disorder that

Amicus Therapeutics to Present at JP Morgan Healthcare Conference  -  Dec 22, 2008
PR Newswire (press release),Amicus has completed Phase 2 clinical trials of Amigal for the treatment of Fabry disease and is conducting Phase 2 clinical trials of Plicera for the

Stem Cells Poised to Grow Organs for Transplant  -  Dec 22, 2008
MarketWatch (press release)Another patient was successfully treated for cardiac sequelae of Fabry's Disease, and is also no longer considered for heart transplant.

BUYINS.NET: Market Maker Surveillance Report. Top 6 Winning Stocks ...  -  Dec 4, 2008
Trading Markets (press release),Fabrazyme, a recombinant form of the human enzyme alpha-galactosidase for the treatment of Fabry disease; Thyrogen, an adjunctive diagnostic agent used

Province revamps drug coverage  -  Dec 8, 2008
Lethbridge Herald,The initial list includes drugs for Fabry disease, Gaucher’s disease, Hunter disease and Pompe disease, along with MPS-I (Hurler/Hurler Scheie).

全?第一???心臟型法布瑞?症發生率高  -  Dec 7, 2008
中時電?報,...法布瑞?症(Fabry disease

Genzyme Beats, Holds to Lowered Guidance  -  23 Jul 2008
TheStreet.comSales of Gaucher disease treatment Cerezyme and Fabry disease treatment Fabrazyme came in at $319 million and $127 million, vs. the Street expectations of

Genzyme Barely Misses Mark, but Revenue Growth Strong  -  23 Jul 2008
TMCnetSales of Cerezyme in Gaucher disease jumped 13 percent to $319.4 million, while Fabrazyme for Fabry disease showed an increase of 21 percent to $126.6

Market Report -- Short Stories (FOLD)  -  23 Jul 2008
MSN MoneyFirm says their industry contacts indicate that a key opinion leader is now consulting Amicus on the development of Amigal for Fabry disease.

CyGene Laboratories Launches StrokeScan(TM) DNA Analysis  -  Jul 21, 2008
MarketWatchFabry disease is a genetic disorder that results in an enzyme deficiency that commonly causes death before age 55 by way of stroke, heart attack or kidney

CyGene to launch new genetic screening test  -  Jul 22, 2008
Trading Markets (press release),Genetic screening of people in high risk groups is essential in order to identify and then diagnose Fabry disease accurately and at an early stage.

Pulmonary Langerhans Cell Histiocytosis and Other Pulmonary ...  -  Jul 16, 2008
RedOrbit,Fabry disease: case report with emphasis on enzyme replacement therapy and possible future therapeutic options. J Dtsch Dermatol Ges. 2007;5:594-597. 75.

Shire offers $521.2 million for Germany's Jerini  -  Jul 3, 2008
CNNMoney.comIn addition to the widely prescribed ADHD drugs Vyvanse and Adderall XR, Shire also makes Replagal for Fabry disease and Elaprase for hunter syndrome.

A Bad Week in Court for US Health Care Organizations  -  Jul 17, 2008
Insurance News Net (press release),...which was intended to treat a rare disorder called Fabry's disease, while hiding the fact it failed a key clinical trial and that he knew federal

Ex-biotech CEO to pay SEC more than $1.1m  -  Jul 10, 2008
Boston Globe,...which was intended to treat a rare disorder called Fabry's disease, while hiding the fact it failed a key clinical trial and that he knew federal

Biotech firm's former CEO to settle SEC suit for $1.2M  -  Jul 11, 2008
SmartBrief,Exchange Commission claiming that he deceived investors by not disclosing the FDA's rejection of Replagal, an experimental treatment for Fabry disease.

Biotech firm's former CEO to settle SEC suit for $1.2M  -  Jul 11, 2008
SmartBrief,Exchange Commission claiming that he deceived investors by not disclosing the FDA's rejection of Replagal, an experimental treatment for Fabry disease.

Fabry sufferers, others with rare conditions mark international ...  -  Feb 29, 2008
ChronicleHerald.ca,Members of the Fabry Disease Society of Nova Scotia are pleased the province has proclaimed the awareness day. Only about 250 Canadians have the rare

VIDEO from Medialink and Shire plc: Rare Diseases Must Be Top of ...  -  Feb 29, 2008
FOXBusinessFabry Disease (also known as Anderson-Fabry Disease) is a lysosomal storage disease with an estimated birth incidence of 1 in 117000.

Amicus Therapeutics Presents Positive Data from Phase 2 Clinical ...  -  Mar 13, 2008
PharmaLive.com (press release),Amicus has completed Phase 2 clinical trials of Amigal(TM) for the treatment of Fabry disease and is conducting Phase 2 clinical trials of Plicera(TM) for

BUYINS.NET: TLB, NGD, CTIC, FOLD, OPXA, PALM Have Been On BUYINS ...  -  Mar 14, 2008
Trading Markets (press release),The company's products include Amigal, which has completed Phase II clinical trial for the treatment of Fabry disease; Plicera, a Phase II clinical trial

Food for Thought  -  Mar 4, 2008
Morris Daily Herald,...“You need to start eating healthy,? the doctor said minutes before I was to undergo my most recent IV treatment for Fabry disease.

Alberta teen pleads for $500000 drug therapy  -  Feb 29, 2008
CBC Ottawa,Koning himself suffers from Fabry disease, a disorder that interferes with the body's ability to break down fatty substances. "It's to make our politicians

SWLA's Children's Miracle Network Champions  -  Mar 18, 2008
KPLC-TV,Nathan and Bradley Rowell were diagnosed three years ago with a rare genetic disorder - in fact, they are the only known twins to have Fabry's disease.



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